At the 15th International Conference on Neuronal Ceroid Lipfuscinosis (Batten Disease) held in Boston, MA, we talked with Sara Mole, PhD of University College London about BATCure - a multidisciplinary and multi-center project to find treatments and/cure for Batten disease.
By the end of the project, the team expects to have:
At least one lead therapy ready for phase 1/2 clinical trial
Developed faster diagnostic tests
A better understanding of the disease and how to better manage peripheral symptoms palliatively.