Rare Disease Report


OCTOBER 07, 2016
Sara Mole, PhD

At the 15th International Conference on Neuronal Ceroid Lipfuscinosis (Batten Disease) held in Boston, MA, we talked with Sara Mole, PhD of University College London about BATCure - a multidisciplinary and multi-center project to find treatments and/cure for Batten disease.  

By the end of the project, the team expects to have:
  • At least one lead therapy ready for phase 1/2 clinical trial
  • Developed faster diagnostic tests
  • A better understanding of the disease and how to better manage peripheral symptoms palliatively.

For more information, visit www.batcure.eu

This article was made possible by a sponsorship from BioMarin Pharmaceutical Inc. Rare Disease Report has sole control over the editorial content.

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