Rare Disease Report

Antisense Therapy and Familial Amyloid Polyneuropathy

MAY 17, 2015

Isis Pharmaceuticals is currently enrolling patients in a phase 3 study to test the safety and efficacy of the antisense drug ISIS-TTRRX in patients with Familial Amyloid Polyneuropathy.

In this interview, Merrill Benson, MD, of Indiana University discusses how the antisense drug works and why so many are interested in the results from this phase 3 study.

For more information, visit http://ttrstudy.com/attr-amyloidosis/

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