Journal Watch: Vimizim Very Effective in Adults with Morquio A
A new study by Hughes et al indicates long-term use of Vimizim (elosulfase afla) in adults with Morquio A is effective and provides those patients with increased strength and endurance to tackle their daily activities.
Dr Koop noted, I think the conversation has to be not through us but between those who create and market the drugs and those who pay the bills.
CRPS is often difficult to diagnose and in Jones’ case, that was also true. His symptoms appeared suddenly while playing high school football.
There is an open debate on the diagnosis and types of the Arnold-Chiari Syndrome (ACHS), joined by the discussion about its treatment and that of the frequently associated idiopathic Syringomyelia (ISM).
Jasmine Lellock ran a marathon to honor her mother, Patti, who passed away from an autoimmune disease called neuromyelitis optica (NMO).
Our home was modified to accommodate the needs of Alternating Hemiplegia of Childhood. AHC will never be welcome, but there are appreciated attributes of it.
With EyeDrive technology, Steve Gleason communicates and maneuvers his wheelchair using his eyes. He wants other ALS patients to have the same opportunities.
Adamas Pharmaceuticals, Inc. will be getting up $100 million from HealthCare Royalty Partners for their drug (ADS-5102) to treat levodopa-induced dyskinesia.
Karen was not diagnosed with Pompe disease until she was 46 years old, even though she had the symptoms of the rare disease for at least 15 years prior.
Excellus BlueCross BlueShield is denying to provide the drug on the basis that the boys are not ambulatory and the drug is 'medically unnecessary'.
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