Lou Gehrig's Disease, or ALS, is an example of neurology as it pertains to rare disease. Turn to Rare Disease for more information about matters of the brain.
RDR Editorial: Deciding the Fate of Charlie Gard
On July 25, the Judge will decide the fate of Charlie Gard. What he decides may lean towards the hippocratic oath: First, do no harm.
As of 18 months after surgery, the child is now able to write, feed, and dress himself more independently and efficiently.
The FDA has approved Aspect Imaging’s MRI unit specifically designed to assess brain and head imaging in neonatal intensive care units.
Intracerebral gene therapy infusions in 4 children with Sanfilippo type B led to sustained enzyme production & improved cognitive functions.
Sarepta is partnering with Clinigen Group to introduce a Managed Access Program for eteplirsen to treat DMD patients amenable to exon 51 skipping.
The safe position would have been to decline the request for fear of liability, error, harm to the unborn, to the parents. We took the case.
Our doctors have been caught between a rock and a hard place knowing PANDAS can be treated but the insurance companies refuse to cover it
Despite being confined to a wheelchair, Friedreich’s ataxia patient Tiffany Gambill crossed off a bucket list item when she completed a 5-mile Spartan Sprint.
If their DMD drug gets approved, Capricor Therapeutics would receive a Priority Review Voucher that is worth millions of dollars.
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