Tommy’s transplanted kidney is, if not the longest, one of the longest functioning live donor kidneys in U.S. history.
At WORLDSymposium, we talked with Elizabeth Smith of Emory University about her poster presentation involving 3 women suspected of having Fabry disease who underwent further genetic testing to confirm or deny the diagnosis.
Just got a sneak peak of the data Alnylam will be presenting next week at the XV International Symposium on Amyloidosis in Uppsala, Sweden.
Kiacta (eprodisate) has had a long history of showing potential for AA amyloidosis then failing to deliver in the end.
The Pan Canadian Pharmaceutical Alliance has called off negotiation with Alexion to allow Soliris to treat Canadians with aHUS.
The Alport Syndrome Foundation (ASF) awarded 3 outstanding Alport syndrome kidney patients the Paul Silver Tribute award.
Attention researchers – you may be eligible to win a $100,000 research grant
The FDA accepted Eisai’s supplemental new drug application for lenvatinib, a potential treatment of patients with advanced or metastatic renal cell carcinoma (RCC) in combination with everolimus, a chemotherapy, following one prior vascular endothelial growth factor (VEGF)-targeted therapy.
Many rare diseases affect the kidneys and the urinary system
Top Orphan Drug Stories for Monday, November 23, 2015