Patients & Caregivers
Conan to Host Rare Disease Fundraiser
Congenital Hyperinsulinism International (CHI) has its annual Sugar Soirée on Sunday, Nov 19, 2017 in NYC. Conan O'Brien will host.
Stem Cell Research and Sickle Cell Disease
Sickle cell anemia or sickle cell disease is due to misshaped red blood cells.
Merkel Cell Carcinoma Treatment Approved in Europe
The European Commission (EC) has approved the first-ever immunotherapy for the rare and aggressive skin cancer metastatic merkel cell carcinoma (mMCC).
Study Administers IMG-7289 to First Patients with Myelofibrosis
The first patients have been dosed in a Phase 1/2 clinical trial of IMG-7289 for the treatment of myelofibrosis (MF), according to Imago BioSciences.
Sancilio Gets Rare Pediatric Disease Designation for Sickle Cell Disease Treatment
Sancilio Pharmaceuticals announced that the FDA has granted Rare Pediatric Disease designation to Altemia Soft Gelatin Capsules for sickle cell disease in children.
Executive Director of TargetCancer Talks Cholangiocarcinoma
Jim Palma sits down with
to discuss cholangiocarcinoma, the disease with which Paul Poth, his brother-in-law and the founder of TargetCancer, was diagnosed.
Somatuline Depot Injection Receives Expanded Approval for Carcinoid Syndrome
Almost 3 years since its approval to treat patients with neuroendocrine tumors, Somatuline Depot has received a supplemental indication to treat carcinoid syndrome.
Aliqopa Gets FDA Approval to Treat Follicular Lymphoma
Accelerated Approval was granted to Bayer Healthcare Pharmaceuticals’ Aliqopa (copanlisib) today for the treatment of follicular lymphoma.
FDA Approves Biosimilar for Cancer Treatment
Amgen’s Mvasi (bevacizumab-awwb), a biosimilar to Avastin, is now FDA-approved for use in adults to treat multiple types of cancer.
New Research Collaboration Aims to Accelerate AML Therapy Research
Daiichi Sankyo and MD Anderson Cancer Center announced a multi-year collaboration dedicated to accelerating the development of novel therapies to treat AML.
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