Raredr

Hematology

Bluebird Bio's Gene Therapy Trial For Sickle Cell and β-Thalassemia
At the 58th ASH meeting in San Diego, CA, we spoke with Dr. Marina Cavazzana PhD about the latest data on bluebird bio’s gene therapy to treat β-thalassemia and sickle cell disease.
Generex Biotechnology plans to buy 51% share of Emmaus Life Sciences, the company that recently submitted an NDA for L-glutamine to treat sickle cell disease.
David Miklos, MD of Stanford University talks about the use of ibrutinib in chronic graft versus host disease.
Saad Usmani, MD, FACP, of the Levine Cancer Institute talks about the convenience and safety of subcutaneous delivery of daratumumab in multiple myeloma patients.
Saad Usmani, MD, FACP, of the Levine Cancer Institute talks about very impressive data showing the efficacy of daratumumab, lenalidomide, and dexamethasone to treat relapsed or refractory multiple myeloma patients.
The FDA issued a warning for cancer patients to not use of the drug PNC-27 which is a non-approved cancer treatment sold online, mostly in other countries.
Pushkal Garg, MD, of Alnylam Pharmaceuticals discusses the recent data on the efficacy and safety of givosiran to treat hepatic porphyrias.
David Kuter, MD of Massachusetts General Hospital talks about the global Gaucher earlier diagnosis consensus (GED-C) initiative that is being developed to help clinicians diagnose many of the Gaucher disease patients that may not be getting properly diagnosed because their symptoms are not as severe.
David Kuter, MD, of Massachusetts General Hospital provides an overview of Gaucher disease and how it is currently managed.
Pushkal Garg, MD, of Alnylam Pharmaceuticals discusses the recent data on the efficacy and safety of fitusiran to treat patients with hemophilia.
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