News
Conferences
Videos
Case Studies
Insights
Interviews
Conditions
Partners
Resource Guide
Newsletter Signup
For Patients
BioPontis Alliance for Rare Diseases
What Rare Diseases Teach Us: Gage's Story
If Not Us, Then Who? A Letter to Henri Termeer
Orphan Drugs and Drug Pricing in 2017
European Reference Networks: Toward a Better Future for Rare Disease patients.
Philanthropy and Impact Investing
Rare Diseases in the Spotlight at EU Level
BioPontis Alliance Develops Translational Research Readiness Tool with Rare Disease Patient Organizations
Integrating Rare Disease Patients into Pre-Clinical Therapy Development. A Workshop Summary Report from BioPontis Alliance for Rare Diseases
MOST POPULAR ARTICLES
First Patient Dosed in X-Linked Retinitis Pigmentosa (XLRP) Treatment
Positive Results from Friedreich's Ataxia Trial Published
FDA Approves Development of VAR 200 for Treatment of FSGS
Can the Epstein-Barr Virus Cause Autoimmune Illnesses?
