Rare Disease Report
Physicians
Physicians
Patients & Caregivers

Mice, Gene Therapy, and Sanfilippo Syndrome

FEBRUARY 28, 2017
Don Clarke, PhD


Don Clarke, Ph.D. of LA BioMed and Phoenix Nest talks about the mouse model they are using to develop a gene therapy for Sanfilippo syndrome.

Copyright © RareDR 2013-2017 Rare Disease Communications. All Rights Reserved.