Top Medical News Today

Senator John McCain Has Brain Cancer
Glioblastoma is the same type of cancer that the late Senator Ted Kennedy had.
Managed Access Program Will Treat Duchenne Patients Amenable to Exon 51 Skipping
Sarepta is partnering with Clinigen Group to introduce a Managed Access Program for eteplirsen to treat DMD patients amenable to exon 51 skipping.
Global Genes Announces 2017 RARE Champions of Hope
Global Genes recently announced the award recipients for 2017 RARE Champions of Hope.
If Not Us, Then Who?  A Letter to Henri Termeer
The safe position would have been to decline the request for fear of liability, error, harm to the unborn, to the parents. We took the case.
Cost-Effective Way to Diagnose Huntington's Disease Coming to Microsoft's Imagine Cup
Team NeuroGate will be competing in the Microsoft Imagine Cup finals with their work that recognizes neurodegenerative disorders like HD and Parkinson’s.
Vertex Stock Soars Following Positive Data from 3 Different Regimens in Cystic Fibrosis Patients
On Tuesday, Vertex Pharmaceuticals announced positive data from Phase 1 and Phase 2 studies of three different triple combination regimens in people with cystic fibrosis (CF) who have one F508del mutation and one minimal function mutation (F508del/Min).
Second FDA Review of Macrilen for AGHD Treatment Monitoring Underway
A Prescription Drug User Fee Act (PDUFA) date is set for December 30, 2017.
Three UK Groups Push to Raise Awareness for Huntington's Disease
Three different groups from the United Kingdom are staying active this week in their efforts to raise awareness of and funds for Huntington’s Disease research.
Illinois Leading the Way for Managing PANDAS
Our doctors have been caught between a rock and a hard place knowing PANDAS can be treated but the insurance companies refuse to cover it
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