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Top Medical News Today

FDA Approves Subcutaneous Version of Rituximab For Several Rare Blood Cancers
The new route of administration can allow patients to be treated within minutes rather than the hours currently needed to administer rituximab intravenously.
New Data Shows Antidepressants in Pregnant Women May Put Newborns at Risk for Hirschprung's
New data show that early maternal use of selective serotonin reuptake inhibitors (SSRIs) could correlate with Hirschsprung’s disease in newborn children.
Rare Disease Report® Forms Strategic Alliance Partnership with 31 Organizations
These collaborations will allow us to spread awareness and help expedite scientific developments for various rare diseases.
IONIS-HTT Rx Study in HD Patients Completes Enrollment
Ionis the completion of enrollment in its Phase 1/2a randomized, placebo-controlled, dose escalation study of IONIS-HTTRs in Huntington’s Disease patients.
Gottlieb's Aggressive Plans to Streamline the Orphan Drug Review Process
FDA Commissioner Scott Gottlieb testified before a Senate Appropriations subcommittee and discussed some of the programs he is implementing to streamline the FDA review
Former Wilms' Tumor Patient Arrives at New York Jets Minicamp
Former hemihypertrophy and Wilms' tumor patient and current nose tackle Mike Pennel arrived at camp last week for his first week on the job as a New York Jet.
Potential Zika Carrying Mosquitoes on the Move
The CDC reports mosquitoes capable of spreading the Zika virus are being found in more areas of the country than initially reported.
Sarepta and Genethon Collaborate on Gene Therapy Research for Duchenne
Sarepta Therapeutics, Inc. and Genethon have signed a gene therapy research collaboration to jointly develop treatments for Duchenne muscular dystrophy (DMD).
NORD's Days of Action Campaign Aims to Protect Healthcare Coverage
NORD has launched the “Days of Action to Protect Your Healthcare Coverage” campaign for protection of health care for children and adults with rare diseases.
Supreme Court Ruling Impacts Where Pharma Companies Can Be Sued
one-fifth of all trials against Johnson & Johnson over talcum powder causing ovarian cancer are in St. Louis. Four trials in that jurisdiction have gone in favor of the plaintiffs.
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